{"id":4490,"date":"2025-11-05T15:30:01","date_gmt":"2025-11-05T15:30:01","guid":{"rendered":"https:\/\/benzifoundation.org\/fondazione-benzi-al-world-orphan-drug-congress-europe-2025\/"},"modified":"2026-04-01T08:46:31","modified_gmt":"2026-04-01T08:46:31","slug":"fondazione-benzi-al-world-orphan-drug-congress-europe-2025","status":"publish","type":"post","link":"https:\/\/benzifoundation.org\/it\/fondazione-benzi-al-world-orphan-drug-congress-europe-2025\/","title":{"rendered":"Fondazione Benzi al World Orphan Drug Congress Europe 2025"},"content":{"rendered":"<p>Fondazione Gianni Benzi ha partecipato al <strong data-start=\"1161\" data-end=\"1198\"><a href=\"https:\/\/www.terrapinn.com\/conference\/world-orphan-drug-congress\/index.stm\" target=\"_blank\" rel=\"noopener\">World Orphan Drug Congress<\/a><\/strong> 2025, che ancora una volta ha riunito istituzioni, industria, ricercatori, autorit\u00e0 regolatorie e organizzazioni di pazienti per affrontare le principali sfide nel campo delle malattie rare.<\/p>\n<p>Viviana Giannuzzi, Responsabile del Dipartimento di Ricerca e Innovazione, ha contribuito al programma con diversi interventi incentrati sugli aspetti regolatori e sulle metodologie di ricerca.<\/p>\n<p>Durante il congresso, Viviana ha preso parte al gruppo di lavoro \u201cCompetizione degli ecosistemi regolatori nell\u2019approvazione dei medicinali: implicazioni politiche nel caso dell\u2019Europa\u201d, condividendo il punto di vista della Fondazione su come le differenze tra i sistemi regolatori possano influenzare lo sviluppo e i percorsi di approvazione dei farmaci orfani. Alla discussione hanno partecipato anche Pedro Franco, Head of Europe Regulatory and Scientific Policy presso Merck, e Violeta Stoyanova-Beninska, Senior Scientific Specialist presso la Human Division dell\u2019EMA, offrendo una panoramica ampia e approfondita del contesto europeo. Viviana ha inoltre presentato una relazione sulle metodologie di ricerca innovative qualificate dall\u2019EMA per le malattie rare, evidenziando come metodi e strumenti innovativi possano supportare lo sviluppo dei farmaci in contesti caratterizzati da popolazioni ridotte e dati limitati.  <\/p>\n<p>Nel corso del congresso, il poster \u201c<strong>An easy-to-use flow chart to classify your clinical study<\/strong>\u201d \u00e8 stato presentato da Maria Luisa Dalessandro. Sviluppato nell\u2019ambito del progetto <a href=\"\/?p=18028\"><strong>BETTER<\/strong><\/a>, finanziato dal Piano Nazionale di Ripresa e Resilienza (PNRR), questo lavoro collaborativo ha ideato e messo a disposizione uno strumento pratico per aiutare ricercatori e clinici a classificare correttamente gli studi clinici dal punto di vista regolatorio nel quadro europeo.. <\/p>\n<p>La partecipazione della Fondazione Gianni Benzi al WODC 2025 riconferma il suo costante impegno nel fare rete per promuovere qualit\u00e0, rigore e innovazione nella ricerca sulle malattie rare e nel contribuire al dialogo europeo sulle questioni regolatorie che hanno un impatto diretto sulla vita dei pazienti.<\/p>\n<p><img loading=\"lazy\" decoding=\"async\" class=\"aligncenter wp-image-21139 size-large\" src=\"https:\/\/benzifoundation.org\/wp-content\/uploads\/2026\/01\/dimensioni-ottimali-per-wordpress-1-1024x853.jpg\" alt=\"\" width=\"1024\" height=\"853\"><\/p>\n","protected":false},"excerpt":{"rendered":"<p>Fondazione Gianni Benzi ha partecipato al World Orphan Drug Congress 2025, che ancora una volta ha riunito istituzioni, industria, ricercatori, autorit\u00e0 regolatorie e organizzazioni di pazienti per affrontare le principali sfide nel campo delle malattie rare. Viviana Giannuzzi, Responsabile del Dipartimento di Ricerca e Innovazione, ha contribuito al programma con diversi interventi incentrati sugli aspetti [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4489,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[224,197,213],"tags":[],"class_list":["post-4490","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-aggiornamenti-dai-progetti","category-erdera","category-eventi"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.3 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Fondazione Benzi al World Orphan Drug Congress Europe 2025 - Fondazione Gianni Benzi - ETS<\/title>\n<meta name=\"description\" content=\"Fondazione Benzi at WODC 2025: insights on EU regulatory ecosystems, innovative rare-disease research methods, and tools.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/benzifoundation.org\/it\/fondazione-benzi-al-world-orphan-drug-congress-europe-2025\/\" \/>\n<meta property=\"og:locale\" content=\"it_IT\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Fondazione Benzi al World Orphan Drug Congress Europe 2025 - 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