Peer Reviewed Journal
Descriptive Analysis of Pediatric Studies Included in the European Union Post-Authorization Study Register from 2010 to 2023
Landi A.; Reggiardo, G.; Didio, A.; D’Ercole, A.; Ceci, A.; Govere, G. S.; Bonifazi, D.; Bonifazi, F.; Crisafulli, S.; Trifirò, G.; Kaguelidou, F.; Hakkarainen, K. M.; Gvozdanović, K.; Barone-Adesi, F.; Ucciero, A.; Felisi, M.
Pediatric Reports; vol. 17, iusse 1, 2025, DOI 10.3390/pediatric17010024
Effects of the Paediatric Regulation funding on the development of off-patent medicines in children
Frontiers in Medicine, Volume 11 - 2024, DOI 10.3389/fmed.2024.1473862
Paediatric-specific content in data standards for health
Turner, M.A.; Kalra, D.; Cornet, R.; Palmeri, A.; Sen, A.; Owen, J.; Pansieri, C.; Lee, J.; Hedley, V.; Nally, S.; Bonifazi, F.; Leary, R.;Straub, V.
Archives of Disease in Childhood Published Online First, 2025,DOI 10.1136/archdischild-2024-327931
Sharing Data and Transferring Samples Within Pediatric Clinical Studies
Landi, A.; D’Ambrosio, F.; Faggion, S.; Rocchi, F.; Paganin, C.; Lain, M. G.; Ceci, A.; Giannuzzi, V.
Healthcare, Volume 12, Issue 23, DOI 10.3390/healthcare12232473
Paediatric formulations—part of the repurposing concept?
Wang, S.; Giannuzzi, V.
Frontiers in Medicine, 11, 2024. DOI 10.3389/fmed.2024.1456247
Design and Implementation of a Sickle Cell Disease Electronic Registry in Resource Limited Setting in Nigeria - A Pilot Study
Idris, M. A.; Ruggieri. L.; Rufai, H. A.; Hassan, A.; Ibrahim. I. N.; Adullahi, F. J.; Awwalu, S.; Nasiru, U.; Bonifazi, F.; Inusa, B.
Hemato, 5(3), 340-349, (2024). DOI 10.3390/hemato5030025
Common conditions of use elements. Atomic concepts for consistent and effective information governance
Sanchez Gonzalez, M.; Kamerling, P.; Iermito, M.; Casati, S.; Riaz, U.; Veal, C.D.; Maini, M.; Jeanson, F.;Benhamed, O.M.; van Enckevort, E.;Landi, A.; Mimouni, Y.; Le Cornec, C.; Coviello, D.A.; Franchin, T.; Fusco, F.; Ramírez García, J.A.;van der Zanden, L.F.M.; Bernier, A.; Wilkinson, M.D.; Mueller, H.; Gibson, S.J.; Brookes, A. J.
Scientific Data, 11, 465 (2024). DOI 10.1038/s41597-024-03279-z
Getting your DUCs in a row - standardising the representation of Digital Use Conditions
Jeanson, F.; Gibson, S. J.; Alper, P.; Bernier, A.; Woolley, J.P.; Mietchen, D.; Strug, A.; Becker, R.; Kamerling, P.; Sanchez Gonzalez, M.; Mah, N.; Novakowski, A.; Wilkinson, M.D.; Benhamed, O.M.; Landi, A.; Krog, G. P.; Müller, H.; Riaz, U.; Veal, C.; Holub, P.; van Enckevort, E.; Brookes, A. J.
Scientific Data, 11, 464 (2024), DOI 10.1038/s41597-024-03280-6
High mortality following early initiation of antiretroviral therapy in infants living with HIV from three African countries
Tagarro, A.; Domínguez-Rodríguez, S.; Cotton, M.; Otwombe, K.;Klein, N.;Lain, M.G.; Nhampossa, T.; Maiga, A. I.; Barnabas, S.; Vaz, P.; Violari, A.; Fernández-Luis, S.; Behuhuma, O.; Sylla, M.; López-Varela, E.; Naniche, D.; Janse-Van-Rensburg, A.; Liberty, A.; Ramsagar, N.;Smit, T.; Makhari, S.; Ismael, N.; Giaquinto, C.;Rossi, P.; Kuhn, L.; Palma, P.; Spyer, M.; Lichterfeld, M.; Nastuoli, E.; Giannuzzi, V.; Ballestero, A.; Cotugno, N.; Morrocchi, E.; Oletto, A.; Traoré, F. T.;Dobbels, E.; Akhalwaya, Y.; Ording-Jespersen, G.; Foster, C.; Rabie, H.; Amuge, P.; Brehin, C.; Pahwa, S.; Coulibaly, Y. A.; Rojo, P.
Science direct.com
Mapping of Data-Sharing Repositories for Paediatric Clinical Research—A Rapid Review
Felisi, M.; Bonifazi, F.; Toma, M.; Pansieri, C.;Leary, R.; Hedley, V.; Cornet, R.; Reggiardo, G.; Landi, A.; D’Ercole, A.; Malik, S.; Nally, S.; Sen, A.; Palmeri, A.; Bonifazi, D.; Ceci, A.
MDPI 2024, 9 issue 4, DOI 10.3390/data9040059
The creation of an adaptable informed consent form for research purposes to overcome national and institutional bottlenecks in ethics review: experience from rare disease registries
Landi, A.; Mimouni, Y.; Giannuzzi, V.; Schaefer, F.; Altavilla, A., Gibson, S.; Daria Julkowska, D.
Front. Med. 2024, 11. DOI 10.3389/fmed.2024.1384026
Learning from conect4children: A Collaborative Approach towards Standardisation of Disease-Specific Paediatric Research Data
Sen, A.; Hedley, V.; Degraeuwe, E.; Hirschfeld, S.; Cornet, R.; Walls, R.; Owen, J.; Robinson, P.N.; Neilan, E.G.; Liener, T.; Nisato, G.; Modi, N.; Woodworth, S.; Palmeri, A.; Gaentzsch, R.; Walsh, M.; Berkery, T.; Lee, J.; Persijn, L.; Baker, K.; An Haack, K.; Segovia Simon, S.; Jacobsen, J. O. B.; Reggiardo, G.; Kirwin, M. A.; Trueman, J.; Pansieri, C.; Bonifazi, D.; Nally, S.; Bonifazi, F.; Leary, R.; Straub, V.
MDPI 2024, 9. DOI: 10.3390/data9040055
Innovative research methodologies in the EU regulatory framework: an analysis of EMA qualification procedures from a paediatric perspective
Giannuzzi, V.; Bertolani, A.; Torretta, S.; Reggiardo, G.; Toich, E.; Bonifazi, D.; Ceci, A.
Front. Med. 2024, 11. DOI: 10.3389/fmed.2024.1369547
Special Issue “Personalized Medicine in Blood Disease of Children”
Ceci, A.; Kountouris, P.; Didio, A.; Bonifazi, F.
Speciale Issue - J. Pers. Med. 2024, 14, 285. DOI: 10.3390/jpm14030285
TISBE: A Public Web Platform for the Consensus-Based Explainable Prediction of Developmental Toxicity
Mastrolorito F, Togo MV, Gambacorta N, Trisciuzzi D, Giannuzzi V, Bonifazi F, Liantonio A, Imbrici P, De Luca A, Altomare CD, Ciriaco F, Amoroso N, Nicolotti O.
Chem. Res. Toxicol. 2024, XX. DOI: 10.1021/acs.chemrestox.3c00310
Dose rationale for gabapentin and tramadol in pediatric patients with chronic pain
Healy P, Verrest L, Felisi M, Ceci A, Della Pasqua O.
Pharmacol Res Perspect. 2023;11:e01138. doi:10.1002/prp2.1138
Target therapy for high-risk neuroblastoma treatment:integration of regulatory and scientific tools is needed
Ceci A, Conte R, Didio A, Landi A, Ruggieri L, Giannuzzi V and Bonifazi F.
Front. Med. 2023;10:1113460. doi: 10.3389/fmed.2023.1113460
Collaborative approach to enhance the knowledge on paediatric rare diseases: the European Paediatric Translational Research Infrastructure. Meeting abstracts from the 11th edition of the European conference on Rare Diseases & Orphan Products (ECRD) 2022
Ruggieri, L.; Ceci, A.; Georgieva, B.; Bertolani, A.; Bartoloni, F.; Bonifazi, F.; Migliaccio, G.; Altavilla, A.; Della Pasqua, O.; Mikros, E.; Kubova, H.; Martelli, P.; Allegaert, K.; Dimitri, P.; Staud, F.; Smits, E.; Kleanthous, M.; Giannattasio, S.; Denora, N.; Tuleu, C.; Bonifazi, D.
Orphanet J Rare Dis 18 (Suppl 1), 118 (2023) P24. https://doi.org/10.1186/s13023-023-02707-4
Off-label is not always off-evidence: authorising paediatric indications for old medicines
de Wildt SN, Foeldvari I, Siapkara A, Lepola P, Kriström B, Ruggieri L, Eichler I, Egger GF
Lancet Child Adolesc Health. 2023 Apr 25:S2352-4642(23)00083-4. doi: 10.1016/S2352-4642(23)00083-4
Reviews in: Regulatory Science
Kerpel-Fronius, S.; Giannuzzi, V.; Stoyanova-Beninska V.; Sun, Z.
Front. Med. Sec. Regulatory Science. Volume 10 - 2023. doi: 10.3389/fmed.2023.1206753
Moving towards a Question-centric approach for regulatory decision-making in the context of drug assessment
Musuamba Tshinanu F, Cheung SYA, Colin P, Davies EH, Barret JS, Pappalardo F, Chappell M, Dogne JM, Ceci A, Della Pasqua O, Rusten IS.
Clin Pharmacol Ther. 2023 Jan 27. doi: 10.1002/cpt.2856
PedCRIN tool for the biosamples management in paediatric clinical trials
Giannuzzi V, Ruggieri L, Conte R, Manfredi C, Felisi M, Kubiak C, Matei M, Malik S, Demotes J, Ceci A, Bonifazi D.
Clin Transl Sci. 2023 Feb 9. doi: 10.1111/cts.13489
The use of real world data for regulatory purposes in the rare diseases setting
Giannuzzi V, Stoyanova-Beninska V and Hivert V
(2022) Editorial. Front. Pharmacol. 13:1089033. doi: 10.3389/fphar.2022.1089033
Random Forest Clustering Identifies Three Subgroups of β-Thalassemia with Distinct Clinical Severity
Vitrano A, Musallam KM, Meloni A, Addario Pollina S, Karimi M, El-Beshlawy A, Hajipour M, Di Marco V, Ansari SH, Filosa A, Ricchi P, Ceci A, Daar S, Vlachaki E, Singer ST, Naserullah ZA, Pepe A, Scondotto S, Dardanoni G, Bonifazi F, Sankaran VG, Vichinsky E, Taher AT, Maggio A, International Working Group on Thalassemia.
Thalassemia Reports. 2022; 12(1):14-23. https://doi.org/10.3390/thalassrep12010004
Overview of the EU PAS register post-authorization studies performed in Europe from September 2010 to December 2018
Sultana J, Crisafulli S, Almas M, Antonazzo IC, Baan E, Bartolini C, Bertuccio MP, Bonifazi F, Capuano A, Didio A, Ehrenstein V, Felisi M, Ferrajolo C, Fontana A, Francisca R, Fourrier-Reglat A, Fortuny J, Gini R, Hyeraci G, Hoeve C, Kontogiorgis C, Isgrò V, Lalagkas PN, L'Abbate L, Layton D, Landi A, Narduzzi S, Pereira LR, Poulentzas G, Rafaniello C, Roberto G, Scondotto G, Sportiello L, Toma M, Toussi M, Verhamme K, Volpe E, Trifirò G.
Pharmacoepidemiol Drug Saf. 2022 Jan 29. doi: 10.1002/pds.5413
Health technology assessment of paediatric medicines: European landscape, challenges and opportunities inside the conect4children project
Moretti F, Ruiz F, Bonifazi F, Pizzo E, Kindblom JM; the c4c HTA expert group.
Br J Clin Pharmacol. 2021 Dec 20. doi: 10.1111/bcp.15190. Epub ahead of print. PMID: 34931373.
Human Microbiome in Children, at the Crossroad of Social Determinants of Health and Personalized Medicine
Sainz T, Pignataro V, Bonifazi D, Ravera S, Mellado MJ, Pérez-Martínez A, Escudero A, Ceci A, Calvo C.
Children. 2021; 8(12):1191. https://doi.org/10.3390/children8121191
Medical Device Development for Children and Young People—Reviewing the Challenges and Opportunities
Dimitri P, Pignataro V, Lupo, M, Bonifazi D, Henke M, Musazzi UM, Ernst F, Minghetti P, Redaelli DF, Antimisiaris SG, Migliaccio G, Bonifazi F, Marciani L, Courtenay AJ, Denora N, Lopedota A.
Pharmaceutics 2021, 13, 2178. https://doi.org/10.3390/pharmaceutics13122178
Informed consent and assent guide for paediatric clinical trials in Europe
Lepola P, Kindred M, Giannuzzi V, Glosli H, Dehlinger-Kremer M, Dalrymple H, Neubauer D, Boylan GB, Conway J, Dewhurst J, Hoffman D.
Arch Dis Child 2021;0:1–9. doi:10.1136/archdischild-2021-322798
Primary HBB gene mutation severity and long-term outcomes in a global cohort of β-thalassaemia
Br J Haematol. 2021 Oct 25. doi: 10.1111/bjh.17897. Epub ahead of print
Survival and causes of death in 2,033 patients with non-transfusion-dependent β-thalassemia
Haematologica. 2021 Sep 1;106(9):2489-2492. doi: 10.3324/haematol.2021.278684. PMID: 33882642; PMCID: PMC8409024.
The International Hemoglobinopathy Research Network (INHERENT): An international initiative to study the role of genetic modifiers in hemoglobinopathies
Kountouris P, Stephanou C, Archer N, Bonifazi F, Giannuzzi V, Kuo KHM, Maggio A, Makani J, Mañú-Pereira MDM, Michailidou K, Nkya S, Nnodu OE, Trompeter S, Tshilolo L, Wonkam A, Zilfalil BA, Inusa BPD, Kleanthous M, on behalf of the International Hemoglobinopathy Research Network (INHERENT).
Am J Hematol. 2021 Aug 18. doi: 10.1002/ajh.26323. Epub ahead of print. PMID: 34406671
Ethical and procedural issues for applying researcher-driven multi-national paediatric clinical trials in and outside the European Union: the challenging experience of the DEEP project
BMC Med Ethics. 2021 Apr 29;22(1):49. doi: 10.1186/s12910-021-00618-2. PMID: 33926431
Paediatric clinical research in Europe: an insight on experts' needs and perspectives
Contemp Clin Trials Commun. 2021 Feb 10;21:100735. doi: 10.1016/j.conctc.2021.100735. PMID: 33665471; PMCID: PMC7905444.
The conect4children (c4c) Consortium: Potential for Improving European Clinical Research into Medicines for Children
Pharm Med (2021). https://doi.org/10.1007/s40290-020-00373-6
Paediatric Medicines in Europe: The Paediatric Regulation—Is It Time for Reform?
Front. Med. 2021 Feb; 8:593281. doi: 10.3389/fmed.2021.593281
A complication risk score to evaluate clinical severity of thalassaemia syndromes
Br J Haematol. 2020 Nov 20. doi: 10.1111/bjh.17203. Epub ahead of print. PMID: 33216983.
European research networks to facilitate drug research in children
Turner M, Cheng K, de Wildt S, Hildebrand H, Attar S, Rossi P, Bonifazi D, Ceci A, Claverol J, Nafria B, Giaquinto C.
Br J Clin Pharmacol. 2020;1–9. DOI: 10.1111/bcp.14545.
Evaluation of the efficacy and safety of deferiprone compared with deferasirox in paediatric patients with transfusion-dependent haemoglobinopathies (DEEP-2): a multicentre, randomised, open-label, non-inferiority, phase 3 trial.
Maggio A, Kattamis A, Felisi M, Reggiardo G, El-Beshlawy A, Bejaoui M, Sherief L, Christou S, Cosmi C, Della Pasqua O, Del Vecchio G, Filosa A, Cuccia L, Hassab H, Kreka M, Origa R, Putti M, Spino M, Telfer P, Tempesta B, Vitrano A, Tsang YC, Zaka A, Tricta F, Bonifazi D, Ceci A.
The Lancet. Haematology. Jun 2020; 7(6):e469-e478. DOI: 10.1016/s2352-3026(20)30100-9
Ethical, Legal and Regulatory Issues of Paediatric Translational Research. Call for an Adequate Model of Governance
Altavilla A, Giannuzzi A, Lupo M, Bonifazi D, Ceci A.
European Journal of Health Law. May 2020. 1–19. https://doi.org/10.1163/15718093-BJA10010
Machine Learning Systems Applied to Health Data and System
Bonifazi F, Volpe E, Digregorio G, Giannuzzi V, Ceci A.
European Journal of Health Law. 2020; 1-17. doi: 10.1163/15718093-BJA10009
Different strategies to execute multi-database studies for medicines surveillance in real world setting: a reflection on the European model
Gini R, Sturkenboom M, Sultana J, Cave A, Landi A, Pacurariu A, Roberto G, Schink T, Candore G, Slattery J, Trifirò G, The Working Group 3 of ENCePP.
Clinical Pharmacology & Therapeutics. April 2020. doi:10.1002/cpt.1833
The Secondary Use of Paediatric Data Under GDPR: Looking for New Safeguards for Research
Altavilla A, Herveg J, Giannuzzi V, Landi A, Ceci A.
European Pharmaceutical Law Review. 2019; Volume 3, Issue 4.156 - 164. https://doi.org/10.21552/eplr/2019/4/6
Survey by TEDDY European Network of Excellence for Paediatric Clinical Research demonstrates potential for Europe‐wide trials
Ruggieri L, Bonifazi D, Landi A, Bonifazi F, Bartoloni F, Costello M, Felisi MG, Gasthuys E, Godo A, Torres FM, Nadal D, Nuytinck L, Rocchi F, Turner M, Ceci A.
Acta Paediatrica. 2019;00:1–6. doi: 10.1111/apa.15020
The “A” of FAIR – As Open as Possible, as Closed as Necessary
Landi A, Thompson M, Giannuzzi V, Bonifazi F, Labastida I, Bonino da Silva Santos LO, Roos M.
Data Intelligence. 2020; 47–55. doi: 10.1162/dint_a_00027
International Comparison of Thalassemia Registries: Challenges and Opportunities
Nori T, Ghazisaeedi M, Aliabad GM, Mehdipour Y, Mehraeen E, Conte R, Safdari R
ACTA INFORM MED. 2019 MAR 27(1): 58-63, doi: 10.5455/aim.2019.27.58-63
An overview of the efficacy and safety of deferiprone in paediatric patients with congenital haemoglobinopathies and chronic iron overload
Ceci A, Conte R, Didio A, Bonifazi D, Felisi M, Giannuzzi V, Bonifazi F.
Expert Opinion on Orphan Drugs. 2019; 7:4,181-197. doi: 10.1080/21678707.2019.1613977
9th European Conference on Rare Diseases & Orphan Products (ECRD Vienna 2018)
Giannuzzi V. Abandoned OMPs.
Orphanet Journal of Rare Diseases. 2018;13(S2)
Safe, Innovative and Accessible Medicines in Europe: A Renewed Strategy for Patients and the Pharmaceutical Sector
Altavilla A.
European Journal of Health Law. 2018;25(2):133-156. DOI: 10.1163/15718093-12520381
A Review on Impact of General Data Protection Regulation on Clinical Studies and Informed Consent
Giannuzzi V, Landi A, Bartoloni F, Ceci A.
J Clin Res Bioeth 2018; 9(3):327. doi: 10.4172/2155-9627.1000327
Investigating the roles and training of paediatric research nurses working across Europe: a questionnaire-based survey
Veal GJ, Malik S, Lupo M, MacFarlane S, Lepola P, Costello M, Ceci A, Boué C, Lecour C, Otto A, Rastegari M, Berry P.
BMJ Paediatr Open. 2017 Sep 5;1(1):e000170 doi: 10.1136/bmjpo-2017-000170
Failures to further developing orphan medicinal products after designation granted in Europe: an analysis of marketing authorisation failures and abandoned drugs
Giannuzzi V, Landi A, Bosone E, Giannuzzi F, Nicotri s, Torrent-Farnell J, Bonifazi F, Felisi M, Bonifazi D, Ceci A.
BMJ Open. 2017 Sep 11;7(9):e017358. doi: 10.1136/bmjopen-2017-017358
The CLOSED trial; CLOnidine compared with midazolam for SEDation of paediatric patients in the intensive care unit: study protocol for a multicentre randomised controlled trial
Neubert A, Baarslag MA, van Dijk M, van Rosmalen J, Standing JF, Sheng Y, Rascher W, Roberts D, Winslade J, Rawcliffe L, Hanning SM, Metsvaht T, Giannuzzi V, Larsson P, Pokorná P, Simonetti A, Tibboel D on behalf of CLOSED Consortium.
BMJ Open. 2017 Nov 8;7(11):e016031corr1. PMID: 28637741; PMCID: PMC5726127.
Orphan medicinal products in Europe and United States to cover needs of patients with rare diseases: an increased common effort is to be foreseen
Giannuzzi V, Conte R, Landi A, Ottomano SA, Bonifazi D, Baiardi P, Bonifazi F, Ceci A.
Orphanet J Rare Dis.2017 Apr 3;12(1):64
The ethical framework for performing research with rare inherited neurometabolic disease patients
Giannuzzi V, Devlieger H, Margari L, Odlind V, Ragab L, Bellettato C et al.
Eur J Pedatr. 2017 Mar;176(3):395-405
Pattern of complications and burden of disease in patients affected by beta thalassemia major
Bonifazi F, Conte R, Baiardi P, Bonifazi D, Felisi M, Giordano P, Giannuzzi V, Iacono A, Padula R, Pepe A, Putti MC, Ruggieri L, Del Vecchio GC, Filosa A, Maggio A, Ceci A on behalf of the HTA-THAL Multiregional Registry.
Curr Med Res Opin. 2017 33(8):1525-1533
Formulating Medicines for children: challenges and issues - La Chimica e l'Industria (3): 2016
D'Andria P, Giannuzzi V, Bonifazi F, Ceci A, Denora N, Altomare C.
The Italian multiregional thalassemia registry: Centers characteristics, services, and patients' population. Hematology
Conte R, Ruggieri L, Gambino A, Bartoloni F, Baiardi P, Bonifazi D, Bonifazi F, Felisi M, Giannuzzi V, Padula R, Pepe A, Putti MC, Del Vecchio GC, Maggio A, Filosa A, Iacono A, Mangiarini L, Ceci A.
2016 Aug;21(7):415-24
Clinical Trial Application in Europe: What Will Change with the New Regulation? Sci Eng Ethics
Giannuzzi V, Altavilla A, Ruggieri L, Ceci A.
2016 Apr;22(2):451-66
Safety Profile of Oral Iron Chelator Deferiprone in Chinese Children with Transfusion-Dependent Thalassaemia
Botzenhardt S, Sing CW, Wong IC, Chan GC, Wong LY, Felisi M, Rascher W, Ceci A, Neubert A.
Curr Drug Saf. 2016;11(2):137-44
Review and evaluation of the methodological quality of the existing guidelines and recommendations for inherited neurometabolic disorders
Cassis L, Cortès-Saladelafont E, Molero-Luis M, Yubero D, González MJ, Ormazábal A, Fons C, Jou C, Sierra C, Ponce EC, Ramos F, Armstrong J, O'Callaghan MM, Casado M, Montero R, Meavilla-Olivas S, Artuch R, Barić I, Bartoloni F, Bellettato CM, Bonifazi F, Ceci A, Cvitanović-Šojat L, Dali CI, D'Avanzo F, Fumic K, Giannuzzi V, Lampe C, Scarpa M, Garcia-Cazorla Á
Orphanet J Rare Dis. 2016; 11: 147. doi: 10.1186/s13023-016-0431-1dis
Successful private-public funding of paediatric medicines research: lessons from the EU programme to fund research into off-patent medicines
Ruggieri L, Giannuzzi V, Baiardi P, Bonifazi F, Davies EH, Giaquinto C, Bonifazi D, Felisi M, Chiron C, Pressler R, Rabe H, Whitaker MJ, Neubert A, Jacqz-Aigrain E, Eichler I, Turner MA, Ceci A; on behalf of the GRiP Consortium.
Eur J Pediatr. 2015; 174(4):481-91
La Rete regionale degli acquisti della Regione Basilicata dall’Health technology assessment alla spesa: presentazione di un case study.
Lorusso S, Chiarolla E, Bonifazi F, Casino D, Sassano S.
Politiche Sanitarie. 2015;16(2):139-149
Multidisciplinary care in haemoglobinopathies. Thalassemia Reports
Ceci A, Mangiarini L, Bonifazi F, Conte R.
2014; 4:4875
Iron chelation therapy in thalassemia major: A systematic review with meta-analyses of 1520 patients included on randomized clinical trials
Maggio A, Filosa A, Vitrano A, Aloj G, Kattamis A, Ceci A, Fucharoen S, Cianciulli P, Grady RW, Prossomariti L, Porter JB, Iacono A, Cappellini MD, Bonifazi F, Cassarà F, Harmatz P, Wood J, Gluud C.
Blood Cells Mol Dis. 2011 Oct 15;47(3):166-75
The management of iron chelation therapy: preliminary data from a national registry of thalassaemic patients
Ceci A, Mangiarini L, Felisi M, Bartoloni F, Ciancio A, Capra M, D'Ascola D, Cianciulli P, Filosa A.
Anemia. 2011;2011:435683
Personalised medicine in paediatrics: individualising treatment in children with rare neurological diseases
Scarpa M, Ceci A, Tomanin R, Mincarone P, Begley D.
EPMA J. 2011 Jun; 2(2): 231–239
Survey of the presence of patulin in fruit juices
Bonerba E, Ceci E, Conte R, Tantillo G.
Food Addit Contam Part B Surveill. 2010;3(2):114‐9
Assessment of dietary intake of patulin from baby foods
Bonerba E, Conte R, Ceci E, Tantillo G.
J Food Sci. 2010 Sep;75(7):T123‐5
Availability of medicines for rare diseases in EU countries
Trama A, Pierannunzio D, Loizzo A, Taruscio D, Ceci A.
Pharmaceuticals Policy and Law, 2009;11(1,2):101-9
Clinical trials for paediatric medicines in Europe
Baiardi P, Girotto S, Della Pasqua O, Harper L, Grosch-Worner I, Ceci A, Giaquinto C.
Pharmaceuticals Policy and Law, 2009;11(1,2):71-78
Recommendation for drug development for children
Catapano M, Manfredi C, Paolucci P, Cross H, Verhamme K, Mellado Pena MJ, Grosch-Worner I, Knibbe C, Ceci A.
Pharmaceuticals Policy and Law, 2009;11(1,2):61-70
The role of paediatric pharmacogenetic studies in Europe
Krekels E, Ceci A, Iolascon A, Girotto S, Della Pasqua O.
Pharmaceuticals Policy and Law, 2009;11(1,2):23-30
Off-label and unlicensed use of medicines for children
Neubert A, Felisi M, Bonifazi A, Manfredi C, Wong ICK, Ceci A.
Pharmaceuticals Policy and Law, 2009;11(1,2):41-49
Defining off-label and unlicensed use of medicines for children: Results of a Delphi survey
Neubert A, Wong IC, Bonifazi A, Catapano M, Felisi M, Baiardi P, Giaquinto C, Knibbe CA, Sturkenboom MC, Ghaleb MA, Ceci A.
Pharmacol Res. 2008 Nov-Dec;58(5-6):316-22
Drugs and food supplements in sports. The nandrolone lessons
Benzi G, Ceci A.
Minerva Pediatr. 2001 Oct;53(5):395-6
Creatine as nutritional supplementation and medicinal product
Benzi G, Ceci A.
J Sports Med Phys Fitness. 2001 Mar;41(1):1-10
