Peer Reviewed Journal

Descriptive Analysis of Pediatric Studies Included in the European Union Post-Authorization Study Register from 2010 to 2023

Landi A.; Reggiardo, G.; Didio, A.; D’Ercole, A.; Ceci, A.; Govere, G. S.; Bonifazi, D.; Bonifazi, F.; Crisafulli, S.; Trifirò, G.; Kaguelidou, F.; Hakkarainen, K. M.; Gvozdanović, K.; Barone-Adesi, F.; Ucciero, A.; Felisi, M.
Pediatric Reports; vol. 17, iusse 1, 2025, DOI 10.3390/pediatric17010024

Effects of the Paediatric Regulation funding on the development of off-patent medicines in children

Ruggieri, L.; Torretta, S.; Giannuzzi, V.; Natale, A.; Felisi, M.; Ceci, A.; Bonifazi, F.
Frontiers in Medicine, Volume 11 - 2024, DOI 10.3389/fmed.2024.1473862

Paediatric-specific content in data standards for health

Turner, M.A.; Kalra, D.; Cornet, R.; Palmeri, A.; Sen, A.; Owen, J.; Pansieri, C.; Lee, J.; Hedley, V.; Nally, S.; Bonifazi, F.; Leary, R.;Straub, V.
Archives of Disease in Childhood Published Online First, 2025,DOI 10.1136/archdischild-2024-327931

Sharing Data and Transferring Samples Within Pediatric Clinical Studies

Landi, A.; D’Ambrosio, F.; Faggion, S.; Rocchi, F.; Paganin, C.; Lain, M. G.; Ceci, A.; Giannuzzi, V.
Healthcare, Volume 12, Issue 23, DOI 10.3390/healthcare12232473

Paediatric formulations—part of the repurposing concept?

Wang, S.; Giannuzzi, V.
Frontiers in Medicine, 11, 2024. DOI 10.3389/fmed.2024.1456247

Design and Implementation of a Sickle Cell Disease Electronic Registry in Resource Limited Setting in Nigeria - A Pilot Study

Idris, M. A.; Ruggieri. L.; Rufai, H. A.; Hassan, A.; Ibrahim. I. N.; Adullahi, F. J.; Awwalu, S.; Nasiru, U.; Bonifazi, F.; Inusa, B.
Hemato, 5(3), 340-349, (2024). DOI 10.3390/hemato5030025

Common conditions of use elements. Atomic concepts for consistent and effective information governance

Sanchez Gonzalez, M.; Kamerling, P.; Iermito, M.; Casati, S.; Riaz, U.; Veal, C.D.; Maini, M.; Jeanson, F.;Benhamed, O.M.; van Enckevort, E.;Landi, A.; Mimouni, Y.; Le Cornec, C.; Coviello, D.A.; Franchin, T.; Fusco, F.; Ramírez García, J.A.;van der Zanden, L.F.M.; Bernier, A.; Wilkinson, M.D.; Mueller, H.; Gibson, S.J.; Brookes, A. J.
Scientific Data, 11, 465 (2024). DOI 10.1038/s41597-024-03279-z

Getting your DUCs in a row - standardising the representation of Digital Use Conditions

Jeanson, F.; Gibson, S. J.; Alper, P.; Bernier, A.; Woolley, J.P.; Mietchen, D.; Strug, A.; Becker, R.; Kamerling, P.; Sanchez Gonzalez, M.; Mah, N.; Novakowski, A.; Wilkinson, M.D.; Benhamed, O.M.; Landi, A.; Krog, G. P.; Müller, H.; Riaz, U.; Veal, C.; Holub, P.; van Enckevort, E.; Brookes, A. J.
Scientific Data, 11, 464 (2024), DOI 10.1038/s41597-024-03280-6

High mortality following early initiation of antiretroviral therapy in infants living with HIV from three African countries

Tagarro, A.; Domínguez-Rodríguez, S.; Cotton, M.; Otwombe, K.;Klein, N.;Lain, M.G.; Nhampossa, T.; Maiga, A. I.; Barnabas, S.; Vaz, P.; Violari, A.; Fernández-Luis, S.; Behuhuma, O.; Sylla, M.; López-Varela, E.; Naniche, D.; Janse-Van-Rensburg, A.; Liberty, A.; Ramsagar, N.;Smit, T.; Makhari, S.; Ismael, N.; Giaquinto, C.;Rossi, P.; Kuhn, L.; Palma, P.; Spyer, M.; Lichterfeld, M.; Nastuoli, E.; Giannuzzi, V.; Ballestero, A.; Cotugno, N.; Morrocchi, E.; Oletto, A.; Traoré, F. T.;Dobbels, E.; Akhalwaya, Y.; Ording-Jespersen, G.; Foster, C.; Rabie, H.; Amuge, P.; Brehin, C.; Pahwa, S.; Coulibaly, Y. A.; Rojo, P.
Science direct.com

 

Mapping of Data-Sharing Repositories for Paediatric Clinical Research—A Rapid Review

Felisi, M.; Bonifazi, F.; Toma, M.; Pansieri, C.;Leary, R.; Hedley, V.; Cornet, R.; Reggiardo, G.; Landi, A.; D’Ercole, A.; Malik, S.; Nally, S.; Sen, A.; Palmeri, A.; Bonifazi, D.; Ceci, A.
MDPI 2024, 9 issue 4, DOI 10.3390/data9040059

The creation of an adaptable informed consent form for research purposes to overcome national and institutional bottlenecks in ethics review: experience from rare disease registries

Landi, A.; Mimouni, Y.; Giannuzzi, V.; Schaefer, F.; Altavilla, A., Gibson, S.; Daria Julkowska, D.
Front. Med. 2024, 11. DOI 10.3389/fmed.2024.1384026

Learning from conect4children: A Collaborative Approach towards Standardisation of Disease-Specific Paediatric Research Data

Sen, A.; Hedley, V.; Degraeuwe, E.; Hirschfeld, S.; Cornet, R.; Walls, R.; Owen, J.; Robinson, P.N.; Neilan, E.G.; Liener, T.; Nisato, G.; Modi, N.; Woodworth, S.; Palmeri, A.; Gaentzsch, R.; Walsh, M.; Berkery, T.; Lee, J.; Persijn, L.; Baker, K.; An Haack, K.; Segovia Simon, S.; Jacobsen, J. O. B.; Reggiardo, G.; Kirwin, M. A.; Trueman, J.; Pansieri, C.; Bonifazi, D.; Nally, S.; Bonifazi, F.; Leary, R.; Straub, V.
MDPI 2024, 9. DOI: 10.3390/data9040055

Innovative research methodologies in the EU regulatory framework: an analysis of EMA qualification procedures from a paediatric perspective

Giannuzzi, V.; Bertolani, A.; Torretta, S.; Reggiardo, G.; Toich, E.; Bonifazi, D.; Ceci, A.
Front. Med. 2024, 11. DOI: 10.3389/fmed.2024.1369547

Special Issue “Personalized Medicine in Blood Disease of Children”

Ceci, A.; Kountouris, P.; Didio, A.; Bonifazi, F.
Speciale Issue -  J. Pers. Med. 2024, 14, 285. DOI: 10.3390/jpm14030285

TISBE: A Public Web Platform for the Consensus-Based Explainable Prediction of Developmental Toxicity

Mastrolorito F, Togo MV, Gambacorta N, Trisciuzzi D, Giannuzzi V, Bonifazi F, Liantonio A, Imbrici P, De Luca A, Altomare CD, Ciriaco F, Amoroso N, Nicolotti O.
Chem. Res. Toxicol. 2024, XX. DOI: 10.1021/acs.chemrestox.3c00310

Dose rationale for gabapentin and tramadol in pediatric patients with chronic pain

Healy P, Verrest L, Felisi M, Ceci A, Della Pasqua O.
Pharmacol Res Perspect. 2023;11:e01138. doi:10.1002/prp2.1138

Target therapy for high-risk neuroblastoma treatment:integration of regulatory and scientific tools is needed

Ceci A, Conte R, Didio A, Landi A, Ruggieri L, Giannuzzi V and Bonifazi F.
Front. Med. 2023;10:1113460. doi: 10.3389/fmed.2023.1113460

Collaborative approach to enhance the knowledge on paediatric rare diseases: the European Paediatric Translational Research Infrastructure. Meeting abstracts from the 11th edition of the European conference on Rare Diseases & Orphan Products (ECRD) 2022

Ruggieri, L.; Ceci, A.; Georgieva, B.; Bertolani, A.; Bartoloni, F.; Bonifazi, F.; Migliaccio, G.; Altavilla, A.; Della Pasqua, O.; Mikros, E.; Kubova, H.; Martelli, P.; Allegaert, K.; Dimitri, P.; Staud, F.; Smits, E.; Kleanthous, M.; Giannattasio, S.; Denora, N.; Tuleu, C.; Bonifazi, D.
Orphanet J Rare Dis 18 (Suppl 1), 118 (2023) P24. https://doi.org/10.1186/s13023-023-02707-4

Off-label is not always off-evidence: authorising paediatric indications for old medicines

de Wildt SN, Foeldvari I, Siapkara A, Lepola P, Kriström B, Ruggieri L, Eichler I, Egger GF
Lancet Child Adolesc Health. 2023 Apr 25:S2352-4642(23)00083-4. doi: 10.1016/S2352-4642(23)00083-4

Reviews in: Regulatory Science

Kerpel-Fronius, S.; Giannuzzi, V.; Stoyanova-Beninska V.; Sun, Z.
Front. Med. Sec. Regulatory Science. Volume 10 - 2023. doi: 10.3389/fmed.2023.1206753

Moving towards a Question-centric approach for regulatory decision-making in the context of drug assessment

Musuamba Tshinanu F, Cheung SYA, Colin P, Davies EH, Barret JS, Pappalardo F, Chappell M, Dogne JM, Ceci A, Della Pasqua O, Rusten IS.
Clin Pharmacol Ther. 2023 Jan 27. doi: 10.1002/cpt.2856

PedCRIN tool for the biosamples management in paediatric clinical trials

Giannuzzi V, Ruggieri L, Conte R, Manfredi C, Felisi M, Kubiak C, Matei M, Malik S, Demotes J, Ceci A, Bonifazi D.
Clin Transl Sci. 2023 Feb 9. doi: 10.1111/cts.13489

The use of real world data for regulatory purposes in the rare diseases setting

Giannuzzi V, Stoyanova-Beninska V and Hivert V
(2022) Editorial. Front. Pharmacol. 13:1089033. doi: 10.3389/fphar.2022.1089033

Random Forest Clustering Identifies Three Subgroups of β-Thalassemia with Distinct Clinical Severity

Vitrano A, Musallam KM, Meloni A, Addario Pollina S, Karimi M, El-Beshlawy A, Hajipour M, Di Marco V, Ansari SH, Filosa A, Ricchi P, Ceci A, Daar S, Vlachaki E, Singer ST, Naserullah ZA, Pepe A, Scondotto S, Dardanoni G, Bonifazi F, Sankaran VG, Vichinsky E, Taher AT, Maggio A, International Working Group on Thalassemia.
Thalassemia Reports. 2022; 12(1):14-23. https://doi.org/10.3390/thalassrep12010004

Overview of the EU PAS register post-authorization studies performed in Europe from September 2010 to December 2018

Sultana J, Crisafulli S, Almas M, Antonazzo IC, Baan E, Bartolini C, Bertuccio MP, Bonifazi F, Capuano A, Didio A, Ehrenstein V, Felisi M, Ferrajolo C, Fontana A, Francisca R, Fourrier-Reglat A, Fortuny J, Gini R, Hyeraci G, Hoeve C, Kontogiorgis C, Isgrò V, Lalagkas PN, L'Abbate L, Layton D, Landi A, Narduzzi S, Pereira LR, Poulentzas G, Rafaniello C, Roberto G, Scondotto G, Sportiello L, Toma M, Toussi M, Verhamme K, Volpe E, Trifirò G.
Pharmacoepidemiol Drug Saf. 2022 Jan 29. doi: 10.1002/pds.5413

Health technology assessment of paediatric medicines: European landscape, challenges and opportunities inside the conect4children project

Moretti F, Ruiz F, Bonifazi F, Pizzo E, Kindblom JM; the c4c HTA expert group.
Br J Clin Pharmacol. 2021 Dec 20. doi: 10.1111/bcp.15190. Epub ahead of print. PMID: 34931373.

Human Microbiome in Children, at the Crossroad of Social Determinants of Health and Personalized Medicine

Sainz T, Pignataro V, Bonifazi D, Ravera S, Mellado MJ, Pérez-Martínez A, Escudero A, Ceci A, Calvo C.
Children. 2021; 8(12):1191. https://doi.org/10.3390/children8121191

Medical Device Development for Children and Young People—Reviewing the Challenges and Opportunities

Dimitri P, Pignataro V, Lupo, M, Bonifazi D, Henke M, Musazzi UM, Ernst F, Minghetti P, Redaelli DF, Antimisiaris SG, Migliaccio G, Bonifazi F, Marciani L, Courtenay AJ, Denora N, Lopedota A.
Pharmaceutics 2021, 13, 2178. https://doi.org/10.3390/pharmaceutics13122178

Informed consent and assent guide for paediatric clinical trials in Europe

Lepola P, Kindred M, Giannuzzi V, Glosli H, Dehlinger-Kremer M, Dalrymple H, Neubauer D, Boylan GB, Conway J, Dewhurst J, Hoffman D.
Arch Dis Child 2021;0:1–9. doi:10.1136/archdischild-2021-322798

Primary HBB gene mutation severity and long-term outcomes in a global cohort of β-thalassaemia

Musallam KM, Vitrano A, Meloni A, Addario Pollina S, Di Marco V, Hussain Ansari S, Filosa A, Ricchi P, Ceci A, Daar S, Vlachaki E, Singer ST, Naserullah ZA, Pepe A, Scondotto S, Dardanoni G, Karimi M, El-Beshlawy A, Hajipour M, Bonifazi F, Vichinsky E, Taher AT, Sankaran VG, Maggio A; International Working Group on Thalassemia (IWG-THAL).
Br J Haematol. 2021 Oct 25. doi: 10.1111/bjh.17897. Epub ahead of print

Survival and causes of death in 2,033 patients with non-transfusion-dependent β-thalassemia

Musallam KM, Vitrano A, Meloni A, Pollina SA, Karimi M, El-Beshlawy A, Hajipour M, Di Marco V, Ansari SH, Filosa A, Ricchi P, Ceci A, Daar S, Vlachaki E, Singer ST, Naserullah ZA, Pepe A, Scondotto S, Dardanoni G, Bonifazi F, Sankaran VG, Vichinsky E, Taher AT, Maggio A.
Haematologica. 2021 Sep 1;106(9):2489-2492. doi: 10.3324/haematol.2021.278684. PMID: 33882642; PMCID: PMC8409024.

The International Hemoglobinopathy Research Network (INHERENT): An international initiative to study the role of genetic modifiers in hemoglobinopathies

Kountouris P, Stephanou C, Archer N, Bonifazi F, Giannuzzi V, Kuo KHM, Maggio A, Makani J, Mañú-Pereira MDM, Michailidou K, Nkya S, Nnodu OE, Trompeter S, Tshilolo L, Wonkam A, Zilfalil BA, Inusa BPD, Kleanthous M, on behalf of the International Hemoglobinopathy Research Network (INHERENT).
Am J Hematol. 2021 Aug 18. doi: 10.1002/ajh.26323. Epub ahead of print. PMID: 34406671

Ethical and procedural issues for applying researcher-driven multi-national paediatric clinical trials in and outside the European Union: the challenging experience of the DEEP project

Giannuzzi V, Felisi M, Bonifazi D, Devlieger H, Papanikolaou G, Ragab L, Fattoum S, Tempesta B, Reggiardo G, Ceci A.
BMC Med Ethics. 2021 Apr 29;22(1):49. doi: 10.1186/s12910-021-00618-2. PMID: 33926431

Paediatric clinical research in Europe: an insight on experts' needs and perspectives

Ruggieri L, Ceci A, Bartoloni F, Elie V, Felisi M, Jacqz-Aigrain E, Lupo M, Malik S, Manfredi C, Reggiardo G, Demotes J, Bonifazi D.
Contemp Clin Trials Commun. 2021 Feb 10;21:100735. doi: 10.1016/j.conctc.2021.100735. PMID: 33665471; PMCID: PMC7905444.

The conect4children (c4c) Consortium: Potential for Improving European Clinical Research into Medicines for Children

Turner MA, Hildebrand H, Fernandes RM, de Wildt SN, Mahler F, Hankard R, Leary R, Bonifazi F, Nobels P, Cheng K, Attar S, Rossi P, Rocchi F, Clavero J, Nafria B, Giaquinto C.
Pharm Med (2021). https://doi.org/10.1007/s40290-020-00373-6

Paediatric Medicines in Europe: The Paediatric Regulation—Is It Time for Reform?

Toma M, Felisi MG, Bonifazi D, Bonifazi F, Giannuzzi V, Reggiardo G, de Wildt S, Ceci A and TEDDY European Network of Excellence for Paediatric Research.
Front. Med. 2021 Feb; 8:593281. doi: 10.3389/fmed.2021.593281

A complication risk score to evaluate clinical severity of thalassaemia syndromes

Vitrano A, Meloni A, Addario Pollina W, Karimi M, El-Beshlawy A, Hajipour M, Di Marco V, Hussain Ansari S, Filosa A, Ricchi P, Ceci A, Daar S, Titi Singer S, Naserullah ZA, Pepe A, Scondotto S, Dardanoni G, Bonifazi F, Vichinsky E, Maggio A.
Br J Haematol. 2020 Nov 20. doi: 10.1111/bjh.17203. Epub ahead of print. PMID: 33216983.

European research networks to facilitate drug research in children

Turner M, Cheng K, de Wildt S, Hildebrand H, Attar S, Rossi P, Bonifazi D, Ceci A, Claverol J, Nafria B, Giaquinto C.
Br J Clin Pharmacol. 2020;1–9. DOI: 10.1111/bcp.14545.

Evaluation of the efficacy and safety of deferiprone compared with deferasirox in paediatric patients with transfusion-dependent haemoglobinopathies (DEEP-2): a multicentre, randomised, open-label, non-inferiority, phase 3 trial.

Maggio A, Kattamis A, Felisi M, Reggiardo G, El-Beshlawy A, Bejaoui M, Sherief L, Christou S, Cosmi C, Della Pasqua O, Del Vecchio G, Filosa A, Cuccia L, Hassab H, Kreka M, Origa R, Putti M, Spino M, Telfer P, Tempesta B, Vitrano A, Tsang YC, Zaka A, Tricta F, Bonifazi D, Ceci A.
The Lancet. Haematology. Jun 2020; 7(6):e469-e478. DOI: 10.1016/s2352-3026(20)30100-9

Ethical, Legal and Regulatory Issues of Paediatric Translational Research. Call for an Adequate Model of Governance

Altavilla A, Giannuzzi A, Lupo M, Bonifazi D, Ceci A.
European Journal of Health Law. May 2020. 1–19. https://doi.org/10.1163/15718093-BJA10010

Machine Learning Systems Applied to Health Data and System

Bonifazi F, Volpe E, Digregorio G, Giannuzzi V, Ceci A.
European Journal of Health Law. 2020; 1-17. doi: 10.1163/15718093-BJA10009

Different strategies to execute multi-database studies for medicines surveillance in real world setting: a reflection on the European model

Gini R, Sturkenboom M, Sultana J, Cave A, Landi A, Pacurariu A, Roberto G, Schink T, Candore G, Slattery J, Trifirò G, The Working Group 3 of ENCePP.
Clinical Pharmacology & Therapeutics. April 2020. doi:10.1002/cpt.1833

The Secondary Use of Paediatric Data Under GDPR: Looking for New Safeguards for Research

 Altavilla A, Herveg J, Giannuzzi V, Landi A, Ceci A.
European Pharmaceutical Law Review. 2019; Volume 3, Issue 4.156 - 164. https://doi.org/10.21552/eplr/2019/4/6

Survey by TEDDY European Network of Excellence for Paediatric Clinical Research demonstrates potential for Europe‐wide trials

Ruggieri L, Bonifazi D, Landi A, Bonifazi F, Bartoloni F, Costello M, Felisi MG, Gasthuys E, Godo A, Torres FM, Nadal D, Nuytinck L, Rocchi F, Turner M, Ceci A.
Acta Paediatrica. 2019;00:1–6. doi: 10.1111/apa.15020

The “A” of FAIR – As Open as Possible, as Closed as Necessary

 Landi A, Thompson M, Giannuzzi V, Bonifazi F, Labastida I,  Bonino da Silva Santos LO, Roos M.
Data Intelligence. 2020; 47–55. doi: 10.1162/dint_a_00027

International Comparison of Thalassemia Registries: Challenges and Opportunities

Nori T, Ghazisaeedi M, Aliabad GM, Mehdipour Y, Mehraeen E, Conte R, Safdari R
ACTA INFORM MED. 2019 MAR 27(1): 58-63, doi: 10.5455/aim.2019.27.58-63

An overview of the efficacy and safety of deferiprone in paediatric patients with congenital haemoglobinopathies and chronic iron overload

Ceci A, Conte R, Didio A, Bonifazi D, Felisi M, Giannuzzi V, Bonifazi F.
Expert Opinion on Orphan Drugs. 2019; 7:4,181-197. doi: 10.1080/21678707.2019.1613977

9th European Conference on Rare Diseases & Orphan Products (ECRD Vienna 2018)

Giannuzzi V. Abandoned OMPs.
Orphanet Journal of Rare Diseases. 2018;13(S2)

Safe, Innovative and Accessible Medicines in Europe: A Renewed Strategy for Patients and the Pharmaceutical Sector

Altavilla A.
European Journal of Health Law. 2018;25(2):133-156. DOI: 10.1163/15718093-12520381

A Review on Impact of General Data Protection Regulation on Clinical Studies and Informed Consent

Giannuzzi V, Landi A, Bartoloni F, Ceci A.
J Clin Res Bioeth 2018; 9(3):327. doi: 10.4172/2155-9627.1000327

Investigating the roles and training of paediatric research nurses working across Europe: a questionnaire-based survey

Veal GJ, Malik S, Lupo M, MacFarlane S, Lepola P, Costello M, Ceci A, Boué C, Lecour C, Otto A, Rastegari M, Berry P.
BMJ Paediatr Open. 2017 Sep 5;1(1):e000170 doi:  10.1136/bmjpo-2017-000170

Failures to further developing orphan medicinal products after designation granted in Europe: an analysis of marketing authorisation failures and abandoned drugs

Giannuzzi V, Landi A, Bosone E, Giannuzzi F, Nicotri s, Torrent-Farnell J, Bonifazi F, Felisi M, Bonifazi D, Ceci A.
BMJ Open. 2017 Sep 11;7(9):e017358. doi: 10.1136/bmjopen-2017-017358

The CLOSED trial; CLOnidine compared with midazolam for SEDation of paediatric patients in the intensive care unit: study protocol for a multicentre randomised controlled trial

Neubert A, Baarslag MA, van Dijk M, van Rosmalen J, Standing JF, Sheng Y, Rascher W, Roberts D, Winslade J, Rawcliffe L, Hanning SM, Metsvaht T, Giannuzzi V, Larsson P, Pokorná P, Simonetti A, Tibboel D on behalf of CLOSED Consortium.
BMJ Open. 2017 Nov 8;7(11):e016031corr1. PMID: 28637741; PMCID: PMC5726127.

Orphan medicinal products in Europe and United States to cover needs of patients with rare diseases: an increased common effort is to be foreseen

Giannuzzi V, Conte R, Landi A, Ottomano SA, Bonifazi D, Baiardi P, Bonifazi F, Ceci A.
Orphanet J Rare Dis.2017 Apr 3;12(1):64

The ethical framework for performing research with rare inherited neurometabolic disease patients

Giannuzzi V, Devlieger H, Margari L, Odlind V, Ragab L, Bellettato C et al.
Eur J Pedatr. 2017 Mar;176(3):395-405

Pattern of complications and burden of disease in patients affected by beta thalassemia major

Bonifazi F, Conte R, Baiardi P, Bonifazi D, Felisi M, Giordano P, Giannuzzi V, Iacono A, Padula R, Pepe A, Putti MC, Ruggieri L, Del Vecchio GC, Filosa A, Maggio A, Ceci A on behalf of the HTA-THAL Multiregional Registry.
Curr Med Res Opin. 2017 33(8):1525-1533

Formulating Medicines for children: challenges and issues - La Chimica e l'Industria (3): 2016

D'Andria P, Giannuzzi V, Bonifazi F, Ceci A, Denora N, Altomare C.

The Italian multiregional thalassemia registry: Centers characteristics, services, and patients' population. Hematology

Conte R, Ruggieri L, Gambino A, Bartoloni F, Baiardi P, Bonifazi D, Bonifazi F, Felisi M, Giannuzzi V, Padula R, Pepe A, Putti MC, Del Vecchio GC, Maggio A, Filosa A, Iacono A, Mangiarini L, Ceci A.
2016 Aug;21(7):415-24

Clinical Trial Application in Europe: What Will Change with the New Regulation? Sci Eng Ethics

Giannuzzi V, Altavilla A, Ruggieri L, Ceci A.
2016 Apr;22(2):451-66

Safety Profile of Oral Iron Chelator Deferiprone in Chinese Children with Transfusion-Dependent Thalassaemia

Botzenhardt S, Sing CW, Wong IC, Chan GC, Wong LY, Felisi M, Rascher W, Ceci A, Neubert A.
Curr Drug Saf. 2016;11(2):137-44

Review and evaluation of the methodological quality of the existing guidelines and recommendations for inherited neurometabolic disorders

Cassis L, Cortès-Saladelafont E, Molero-Luis M, Yubero D, González MJ, Ormazábal A, Fons C, Jou C, Sierra C, Ponce EC, Ramos F, Armstrong J, O'Callaghan MM, Casado M, Montero R, Meavilla-Olivas S, Artuch R, Barić I, Bartoloni F, Bellettato CM, Bonifazi F, Ceci A, Cvitanović-Šojat L, Dali CI, D'Avanzo F, Fumic K, Giannuzzi V, Lampe C, Scarpa M, Garcia-Cazorla Á
Orphanet J Rare Dis. 2016; 11: 147. doi:  10.1186/s13023-016-0431-1dis

Successful private-public funding of paediatric medicines research: lessons from the EU programme to fund research into off-patent medicines

Ruggieri L, Giannuzzi V, Baiardi P, Bonifazi F, Davies EH, Giaquinto C, Bonifazi D, Felisi M, Chiron C, Pressler R, Rabe H, Whitaker MJ, Neubert A, Jacqz-Aigrain E, Eichler I, Turner MA, Ceci A; on behalf of the GRiP Consortium.
Eur J Pediatr. 2015; 174(4):481-91

La Rete regionale degli acquisti della Regione Basilicata dall’Health technology assessment alla spesa: presentazione di un case study.

Lorusso S, Chiarolla E, Bonifazi F, Casino D, Sassano S.
Politiche Sanitarie. 2015;16(2):139-149

Multidisciplinary care in haemoglobinopathies. Thalassemia Reports

Ceci A, Mangiarini L, Bonifazi F, Conte R.
2014; 4:4875

Iron chelation therapy in thalassemia major: A systematic review with meta-analyses of 1520 patients included on randomized clinical trials

Maggio A, Filosa A, Vitrano A, Aloj G, Kattamis A, Ceci A, Fucharoen S, Cianciulli P, Grady RW, Prossomariti L, Porter JB, Iacono A, Cappellini MD, Bonifazi F, Cassarà F, Harmatz P, Wood J, Gluud C.
Blood Cells Mol Dis. 2011 Oct 15;47(3):166-75

The management of iron chelation therapy: preliminary data from a national registry of thalassaemic patients

Ceci A, Mangiarini L, Felisi M, Bartoloni F, Ciancio A, Capra M, D'Ascola D, Cianciulli P, Filosa A.
Anemia. 2011;2011:435683

Personalised medicine in paediatrics: individualising treatment in children with rare neurological diseases

Scarpa M, Ceci A, Tomanin R, Mincarone P, Begley D.
EPMA J. 2011 Jun; 2(2): 231–239

Survey of the presence of patulin in fruit juices

Bonerba E, Ceci E, Conte R, Tantillo G.
Food Addit Contam Part B Surveill. 2010;3(2):114‐9

Assessment of dietary intake of patulin from baby foods

Bonerba E, Conte R, Ceci E, Tantillo G.
J Food Sci. 2010 Sep;75(7):T123‐5

Availability of medicines for rare diseases in EU countries

Trama A, Pierannunzio D, Loizzo A, Taruscio D, Ceci A.
Pharmaceuticals Policy and Law, 2009;11(1,2):101-9

Clinical trials for paediatric medicines in Europe

Baiardi P, Girotto S, Della Pasqua O, Harper L, Grosch-Worner I, Ceci A, Giaquinto C.
Pharmaceuticals Policy and Law, 2009;11(1,2):71-78

Recommendation for drug development for children

Catapano M, Manfredi C, Paolucci P, Cross H, Verhamme K, Mellado Pena MJ, Grosch-Worner I, Knibbe C, Ceci A.
Pharmaceuticals Policy and Law, 2009;11(1,2):61-70

The role of paediatric pharmacogenetic studies in Europe

Krekels E, Ceci A, Iolascon A, Girotto S, Della Pasqua O.
Pharmaceuticals Policy and Law, 2009;11(1,2):23-30

Off-label and unlicensed use of medicines for children

Neubert A, Felisi M, Bonifazi A, Manfredi C, Wong ICK, Ceci A.
Pharmaceuticals Policy and Law, 2009;11(1,2):41-49

Defining off-label and unlicensed use of medicines for children: Results of a Delphi survey

Neubert A, Wong IC, Bonifazi A, Catapano M, Felisi M, Baiardi P, Giaquinto C, Knibbe CA, Sturkenboom MC, Ghaleb MA, Ceci A.
Pharmacol Res. 2008 Nov-Dec;58(5-6):316-22

Drugs and food supplements in sports. The nandrolone lessons

Benzi G, Ceci A.
Minerva Pediatr. 2001 Oct;53(5):395-6

Creatine as nutritional supplementation and medicinal product

Benzi G, Ceci A.
J Sports Med Phys Fitness. 2001 Mar;41(1):1-10

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